EXPLORE Natural History Study Data Published in “Hepatology”

EXPLORE Natural History Study Data Published in “Hepatology”

We published results from the EXPLORE natural history study of more than 100 acute hepatic porphyria (AHP) patients with recurrent attacks in Hepatology in a paper titled, “EXPLORE: A Prospective, Multinational, Natural History Study of Patients with Acute Hepatic Porphyria with Recurrent Attacks.”

Read the paper in Hepatology

In EXPLORE, patients experienced attacks often requiring treatment in a healthcare facility and/or with hemin, as well as chronic symptoms that adversely influence day-to-day functioning. The high disease burden and diminished quality of life in this study population highlight the need for novel therapies.


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