Your search has returned a large number of results. Try searching for a more specific term or phrase.

Patient Advocacy

Patients PATIENT ADVOCACY At Alnylam, we believe that patients are experts in their experience. They are at the center of everything we do and every decision we make. We are grateful to work alongside advocacy groups around the world,…, Patient Advocacy Around the World Working in more than 20 countries with over 60 Patient Advocacy Groups (PAGs) ADVOCACY GROUP LEGEND:   Acute Hepatic Porphyria   Hereditary ATTR Amyloidosis   Primary…

Genetic Testing and Counseling Program

Patients NO-CHARGE GENETIC TESTING AND COUNSELING PROGRAM Alnylam Act® Alnylam Act® is a sponsored, no-charge, third-party genetic testing and counseling program for people with a family history or suspected diagnosis of certain genetic…, Watch the Alnylam Act® Video Introduction , What Is Genetic Testing? Genetic testing can identify changes to DNA that may lead to a genetic condition. Results of a genetic test can confirm or rule out a suspected genetic disease or help determine someone’s chance of developing or passing…

Patient Services

Patients PATIENT SERVICES Here for You At Alnylam, we believe in going further than providing treatment options. That’s why we’ve established comprehensive support programs for those affected by the diseases we focus on. , Access To Investigational Medicines Here at Alnylam, we all live by a shared philosophy when it comes to patient access: our therapies must get to those who will benefit from them. We consider this philosophy our compass, guiding how we will…

Primary Hhyperoxaluria

Patients PRIMARY HYPEROXALURIA Understanding Primary Hyperoxaluria Type 1 Primary hyperoxaluria (PH) constitutes a group of rare inherited disorders of the liver characterized by the overproduction of oxalate, an end-product of…, What Are The Symptoms Of PH1? People with PH1 often experience the formation of oxalate stones throughout the urinary tract and kidneys. When a person with PH1 has a kidney stone, symptoms can include: Flank pain Painful …, Ph1 Inside The Body , Understanding PH1: One family’s story Three of Jared and Natalie’s four children were born with PH1. Hear from Claire and Benson about what it’s like to live with this rare inherited disorder.

Acute Hepatic Porphyria

Patients ACUTE HEPATIC PORPHYRIA Understanding Acute Hepatic Porphyria Acute hepatic porphyria (AHP) refers to a family of ultra-rare, genetic diseases characterized by potentially life-threatening attacks and, for some patients, chronic…, Acute Hepatic Porphyria Symptoms Can Impact Quality of Life Affected individuals can experience some combination of the following symptoms: Severe, diffuse abdominal pain, vomiting/nausea, dark/reddish urine, hyponatremia Muscle weakness…, Acute Hepatic Porphyria Symptoms Can Impact Quality of Life Affected individuals can experience some combination of the following symptoms: Severe, diffuse abdominal pain, vomiting/nausea, dark/reddish urine, hyponatremia…, What Causes Acute Hepatic Porphyria? , What causes acute hepatic porphyria?         In people with the genetic defect for AHP, one of the enzymes in the pathway that creates heme is deficient. Certain triggers can impact the pathway and can cause an…, What Is It Like to Live With and Care for a Person With Acute Hepatic Porphyria (AHP)?

Lumasiran Early Access

Medical Professionals EARLY ACCESS PROGRAM FOR LUMASIRAN Lumasiran is a subcutaneously administered RNAi therapeutic targeting hydroxyacid oxidase 1 (HAO1)—the gene encoding glycolate oxidase (GO)—for the treatment of primary hyperoxaluria…

Early Access Program

Medical Professionals ACCESS TO INVESTIGATIONAL THERAPIES Helping Eligible Patients Gain Access to Alnylam Investigational Therapies Alnylam is dedicated to developing new therapies that have a positive impact on patient health, and to…, Early Access Programs Currently Open

Genetic Testing & Counseling

Medical Professionals GENETIC TESTING AND COUNSELING PROGRAM Alnylam Act® Alnylam Act® is a sponsored, no-charge, third party genetic testing and counseling program for patients with a family history or suspected diagnosis of hereditary…, How Genetic Counseling Works Genetic counseling is an optional service available to patients in the U.S. and Canada that provides information and support for patients who have, or may be at risk for, genetic conditions. Genetic counselors are…

Medical Professional Resources

Medical Professionals INFORMATION FOR MEDICAL PROFESSIONALS Alnylam is committed to supporting and partnering with the healthcare community across the disease areas in which we work. We actively engage with medical professionals through our…, Our robust pipeline of investigational RNAi therapeutics is currently focused on several disease areas including transthyretin amyloidosis, rare diseases, cardiovascular diseases, metabolic diseases, and neurological diseases. , Alnylam Grant Information Alnylam is committed to supporting the medical and scientific understanding of our therapeutic areas of interest for healthcare professionals. Additionally, we are committed to supporting educational programs and…

404 not found

The page you are looking for is not found The page you are looking for does not exist. It may have been moved, or removed altogether. Perhaps you can return back to the site’s homepage and see if you can find what you are looking for.…