RESOURCES FOR MEDICAL PROFESSIONALS

We Work to Give Medical Professionals the Tools They Need

Alnylam is committed to supporting and partnering with the healthcare community, across many disease areas. This includes providing information on our research and treatments in development.

Illustrated Scientific Diagram Of The Natural Process of RNAi

Acting “Upstream” of Today’s Medicines

With investigational RNAi therapeutics, we believe it may be possible to block the production of disease-causing proteins before they are made.

More About RNAi ›

OUR

PIPELINE

Late Stage

Learn more about our investigational therapies in hereditary ATTR amyloidosis, hemophilia, acute hepatic porphyria, and primary hyperoxaluria type 1.

Early Stage

Learn more about our investigational therapies across multiple disease areas.

Alnylam Grant Information

Alnylam is committed to supporting the medical and scientific understanding of our therapeutic areas of interest for healthcare professionals. Additionally, we are committed to supporting educational programs and initiatives spearheaded by organizations focused on patient advocacy, community education and support, and other scientific efforts related to our therapeutic areas of interest. To learn more about grants, sponsorships, or how to submit a grants request, visit our grants page.

Access to Investigational Medicines

Alnylam is dedicated to developing new therapies that have a positive impact on patient health, and to serving patients, patient families, and patient communities through education, empathy, and awareness. We understand that there are seriously ill patients who will not be eligible for our clinical trials and may not have options for alternative therapies, including investigational therapies in trials being conducted by other sponsors. In these circumstances, Alnylam will consider providing a requesting physician with pre-approval access to a specific Alnylam investigational medicine, for the treatment of an individual patient outside of a clinical trial, when certain conditions are met.

 

To read our statement on access to investigational medicines, click here.

Onpattro (Patisiran) - Approved For Patients In The US

APPROVED IN THE U.S.

Learn more about an FDA-approved treatment option available for patients in the U.S.
Learn More ›

Alnylam Assist Case Manager With Headset

ALNYLAM ASSIST®

Alnylam Assist® helps patients access ONPATTRO® (patisiran) with personalized support.
Visit Site ›

Alnylam Act - No-Charge Genetic Testing - Woman

ALNYLAM ACT

Alnylam Act provides no-charge, independent genetic testing and counseling to individuals in the US and Canada who may have hATTR amyloidosis, acute hepatic porphyria, or primary hyperoxaluria type 1 (PH1).

Get More Info ›

Acute Hepatic Porphyria (AHP) - Illustration Of The Path To Diagnosis

ACUTE HEPATIC PORPHYRIA (AHP)

Learn more about the signs and symptoms of AHP, and how to guide your patients to a clear diagnosis.
Start Here ›

SIGN UP FOR EMAIL UPDATES

Receive news and updates on the work at Alnylam that affects you most.